Regulators have opened a one-time gene therapy to some of the youngest patients with sickle cell disease. On July 1, 2026, ...
After living with the most severe form of sickle cell disease for 17 years, a Knoxville teen is undergoing a groundbreaking ...
A Nashville doctor helped pioneer an FDA approved "state-of-the-art" gene-editing therapy that could be a cure for painful ...
The rapid progression of genetic engineering, regenerative medicine, and pharmacology has positioned gene, cell, and ...
The curing sickle cell through gene therapy story is a long way from being written. But it’s for sure that it has not gone ...
Gene editing has delivered remarkable results against sickle cell disease. Now researchers are working to make these personalized treatments faster, cheaper, and available to far more patients.
Learn how gene editing is transforming sickle cell disease treatment and why expanding access to younger children matters.
The Food and Drug Administration recently approved gene therapy to treat sickle cell disease among children ages 2 and older, which a Nashville doctor described as a medical milestone.
Gene therapy has changed what is possible for people living with sickle cell disease. New treatments have shown that the ...
Cell and gene therapies, or CGT, have come a long way since they were first introduced. In the last few decades, both cell therapy—the transplantation of living cells—and gene therapy—the use of ...
Among the first projects identified under the partnership is a Phase 2 extension study evaluating the safety and efficacy of ...
Digitized R&D workflows help cell therapy developers reduce manual data handling and accelerate biologics development.